A Phase 1 Gene Therapy Study for Alpha-1 Antitrypsin Deficiency

Recruiting Phase 1 NCT06996756

Study Description

Investigating a Gene Therapy Treatment for Alpha-1 Antitrypsin Deficiency

Study Details

Registry ID:
NCT06996756
Conditions:
Alpha 1-Antitrypsin Deficiency
Phase:
Phase 1
Target Enrollment:
16 participants
Start Date:
Age Range:
18–70 years
Healthy Volunteers:
No

Study Locations (1 site)

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